Stuart Cobb
Neurogene
About this speaker
Stuart Cobb heads a translational research laboratory that is focused on developing genetic therapies for severe neurological and neurodevelopmental disorders, notably Rett syndrome. His research aims to address the tractability of severe brain disease to genetic rescue and to develop innovative therapeutic solutions for clinical translation. His research highlights include the original genetic rescue results in Rett syndrome, and his group was the first to report the ameliorative effect of gene therapy in mice modelling the disorder. His laboratory has developed a number of novel gene therapy approaches optimized for efficacy and safety. This includes the development of regulated expression cassettes and RNA based approaches. He was a founding member of the Rett Syndrome Research Trust Gene Therapy Consortium. Since late 2018 he has been Chief Scientific Officer at Neurogene, a genetic therapy company focusing on rare neurological disease.
